Earlier and higher dosing of alglucosidase alfa improve outcomes in patients with infantile-onset Pompe disease: Evidence from real-world experiences
- Yin Hsiu Chien
- , Wen Hui Tsai
- , Chaw Liang Chang
- , Pao Chin Chiu
- , Yen Yin Chou
- , Fuu Jen Tsai
- , Siew Lee Wong
- , Ni Chung Lee
- , Wuh Liang Hwu
Research output: Contribution to journal › Article › peer-review
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